Status | Study |
Terminated |
Study Name: Allo-HCT MUD for Non-malignant Red Blood Cell (RBC) Disorders: Sickle Cell, Thal, and DBA: Reduced Intensity Conditioning, Co-tx MSCs Condition: Sickle Cell Disease Thalassemia Diam Date: 2009-08-12 Interventions: Procedure: Bone marrow transplantation |
Completed |
Study Name: Magnetic Resonance Imaging (MRI) Assessments of the Heart and Liver Iron Load in Patients With Transfusion Induced Iron Overload Condition: Hemoglobinopathies Myelodysplastic Syndromes Other Inherit Date: 2008-05-05 Interventions: Drug: deferasirox Deferasirox up to 40mg/kg/day, PO, Dispersible tablets, taken once daily |
Completed |
Study Name: Busulfan, Antithymocyte Globulin, and Fludarabine Followed By a Donor Stem Cell Transplant in Treating Young Patients With Blood Disorders, Bone Marrow Disorders, Chronic Myelogenous Leukemia in First Chronic Phase, or Acute Myeloid Leukemia in First Remission Condition: Congenital Amegakaryocytic Thrombocytopenia Diamond-blackfan Anemia Date: 2006-03-21 Interventions: Biological: anti-thymocyte globulin Drug: |
Completed |
Study Name: Alemtuzumab, Fludarabine, and Busulfan Followed By Donor Stem Cell Transplant in Treating Young Patients With Hematologic Disorders Condition: Congenital Amegakaryocytic Thrombocytopenia Diamond-blackfan Anemia Date: 2006-03-09 Interventions: Biological: alemtuzumab Drug: busulfan |
Terminated |
Study Name: Donor Umbilical Cord Blood Transplant in Treating Patients With Hematologic Cancer Condition: Chronic Myeloproliferative Disorders Diamond-blackfan Anemia Date: 2006-02-09 Interventions: Drug: anti-thymocyte globulin Drug: busulf |
Completed |
Study Name: Partially Matched Stem Cell Transplantation for Patients With Refractory Severe Aplastic Anemia or Refractory Cytopenias Condition: Anemia, Aplastic Amegakaryocytic Thrombocytopenia Date: 2005-10-24 Interventions: Device: Allogeneic stem cell transplant Participants will receive a reduced intensity conditioning regim |
Completed |
Study Name: Expanded Access of Deferasirox to Patients With Congenital Disorders of Red Blood Cells and Chronic Iron Overload Condition: Thalassemia Sickle Cell Disease Diam Date: 2005-10-06 Interventions: Drug: Deferasirox 125 mg, 250 mg and 500 mg tablets. Dosage was calculated based on participant's body w |
Completed |
Study Name: Rituximab to Treat Moderate Aplastic Anemia, Pure Red Cell Aplasia, or Diamond Blackfan Anemia Condition: Anemia, Aplastic Red-Cell Aplasia, Pure Anemia, Diamond-Bl Date: 2005-09-29 Interventions: Drug: Rituximab Rituximab (Rituxan) 375mg/m2 intravenous infusion. The infusion will be once every week |
Completed |
Study Name: Stem Cell Transplant for Bone Marrow Failure Syndromes Condition: Diamond-Blackfan Anemia Kostmann's Neutropenia Date: 2005-09-12 Interventions: Procedure: Stem cell transplant |
Active, not recruiting |
Study Name: Stem Cell Transplant for Hemoglobinopathy Condition: Sickle Cell Disease Thalassemia Severe Congenital Neutrope Date: 2005-09-12 Interventions: Drug: Busulfan, Fludarabine, ATG, TLI |